Genetics

A team of researchers at CHOP and the Perelman School of Medicine developed a personalized gene-editing treatment for a baby’s rare disorder, using CRISPR to alter his DNA.

Kiran Musunuru and Rebecca Ahrens-Nicklas of the Perelman School of Medicine led a team from Penn and the Children’s Hospital of Philadelphia that used gene editing to heal a baby with a rare genetic condition.

César de la Fuente of the Perelman School of Medicine, School of Engineering and Applied Science, and School of Arts & Sciences and colleagues are probing genetic remnants of Neanderthals and extinct animals to find new antibiotics.

Frederick Kaplan of the Perelman School of Medicine shares his experience treating a patient with an unusual case of FOP, a rare genetic condition that causes the growth of a “second skeleton.”

Kiran Musunuru and Rebecca Ahrens-Nicklas of the Perelman School of Medicine led a team from Penn and the Children’s Hospital of Philadelphia that used gene editing to heal a baby with a rare genetic condition.

Kiran Musunuru and Rebecca Ahrens-Nicklas of the Perelman School of Medicine led a team from Penn and the Children’s Hospital of Philadelphia that used gene editing to heal a baby with a rare genetic condition.

Kiran Musunuru and Rebecca Ahrens-Nicklas of the Perelman School of Medicine led colleagues at Penn and the Children’s Hospital of Philadelphia to treat a baby with a rare genetic disorder using a customized gene-editing treatment.